Rare & hard-to-treat diseases

Hemophilia & gene therapy

Hospitals in China recommended for Hemophilia & gene therapy, with Fudan specialty rankings and sources. Related specialties: Hematology, Rare Diseases.

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Last updated: 2026-11-03

Related specialties: Hematology · Rare Diseases
Also known as: hemophilia A, hemophilia B, gene therapy

Recommended hospitals

Hospitals are listed in order of recommendation, based on the Fudan specialty reputation ranking and published sources. This is not medical advice.

1
Institute of Hematology & Blood Diseases Hospital, Chinese Academy of Medical Sciences
TianjinGrade 3A Public HospitalHematology #2International patient department
Led phase 1-3 clinical trials of hemophilia B gene therapy BBM-H901, results published in Nature Medicine and approved by NMPA for marketing, Asia's first liver-targeted gene therapy product; Ranked #2 in the 2023 Fudan Hematology specialty reputation ranking
Sources: rank.cn-healthcare.com pharnexcloud.com
2
Ruijin Hospital, Shanghai Jiao Tong University School of Medicine
ShanghaiGrade 3A Public HospitalHematology #3International patient department
A++++ in Fudan hospital comprehensive ranking, hematology department contributed to China hemophilia gene therapy clinical application guidelines with comprehensive gene therapy capability; Ranked #3 in the 2023 Fudan Hematology specialty reputation ranking
Sources: rank.cn-healthcare.com sohu.com
3
Peking Union Medical College Hospital
BeijingGrade 3A Public HospitalRare Diseases #1International patient department
Participated in multicenter clinical trials of hemophilia B gene therapy, national key clinical specialty in hematology, supported by rare disease MDT platform for gene therapy follow-up; Ranked #1 in the 2023 Fudan Rare Diseases specialty reputation ranking
Sources: rank.cn-healthcare.com pumch.cn
4
Peking University People's Hospital
BeijingGrade 3A Public HospitalHematology #1International patient department
Ranked #1 in the 2023 Fudan Hematology specialty reputation ranking
Sources: rank.cn-healthcare.com
5
West China Hospital of Sichuan University
ChengduGrade 3A Public HospitalRare Diseases #4International patient department
Ranked #4 in the 2023 Fudan Rare Diseases specialty reputation ranking
Sources: rank.cn-healthcare.com
6
The First Affiliated Hospital of Zhejiang University School of Medicine
HangzhouGrade 3A Public HospitalHematology #6International patient department
Ranked #6 in the 2023 Fudan Hematology specialty reputation ranking
Sources: rank.cn-healthcare.com

Other notable hospitals

The Second Affiliated Hospital of Kunming Medical UniversityAs key collaborating site completed phase 3 data verification for hemophilia B gene therapy published in Nature Medicine, hematology department qualified for gene therapykyfey.com

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